RICKETS AND THE KIDNEYS

This is indeed a difficult and fairly complex subject, but I will try to explain it as simply as I can.

When one builds up waste products in the body from protein, one of the wastes is phosphate. This chemical is found in large amounts in most proteins and, therefore, needs to excreted in the urine in large amounts. When the filters aren't functioning, it builds up in the body ( usually when kidney function is down to one-third of normal or less).

As phosphate builds up, certain mechanisms work to make calcium go down (most is probably excreted in the urine) to keep a balance in the two. When the blood calcium gets down, a gland in your neck called the parathyroid is turned on, producing a chemical parathyroid hormone which, among other things, releases calcium from bones, in or to bring the blood calcium back up. However, since the phosphate is elevated, the calcium is rapidly excreted (since one cannot lower the phosphate and the calcium and phosphate operate in opposite directions, the calcium must come down). This complex action causes a steady loss of calcium from the bones (secondary hyperparathyroidism), thereby weakening them (it's kind of like removing the walls from girders of the building: after a while it is not functional).

Another problem deals with Vitamin D. In order to replace the calcium being lost, one needs to absorb the calcium in what one eats. One needs Vitamin D, which is activated by sunlight and then made more active, first by the liver and then by the kidney. Comparably, the Vitamin D one eats has a function of approximately "one", after the liver it is "two" and after the kidney it is "one hundred". The activation of Vitamin D occurs in the tubules (which are defective) and, therefore, the cystinotic does not have active Vitamin D to absorb calcium from the intestines to replace body losses. Rickets result from the active Vitamin D deficiency.

How does the physician stop this progressive renal osteodystophy (bone disease caused by kidney disease)? Usually one can control this process by giving medication during meals to bind phosphate, so it not absorbed and the process is stopped early. Frequently this is not enough, however, and calcium and a Vitamin D product need tobe given so there is adequate calcium absorbed to be put back into bones and keep them growing. Without treatment, the bones become very painful, the patient usually refuses to walk, the bones hurt, and the child becomes very irritable and might even refuse to be held. The bones become brittle, with bowing of the legs, widening of the wrists and ankles and multiple small fractures which occur even without trauma. As a consequence, there is a slowing or absence of growth.

The fine balance of these medications and the interplay of calcium, phosphorous and Vitamin D on bones, kidneys and the intestines unfortunately requires frequent blood testing and changes in medicine and is a difficult task. In my experience, this needs to be supervised by a physician experienced and skilled in this area, in order to prevent the consequences of these metabolic problems.


Sheldon Orloff, MD Sub-Chief of Renal Medicine/Kaiser Hospitals

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